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14 Jun 2012

What is pharmalogical treatment?

Illustration for article: What is pharmalogical treatment?
The French Muscular Dystrophy Association (AFM-Téléthon) supports research into new molecules as well as existing pharmacological treatments, the potential of which has never been explored for neuromuscular diseases or rare diseases.

New pharmacological treatments

Today, the term 'drug' covers both classic pharmacological agents produced by chemical synthesis or extracts of natural products, and cell and gene therapy products.

There are two sorts of research into "classic" drugs. Firstly, to find new active molecules, notably by screening banks, and secondly to find new indications for existing molecules.

Certain molecules are already available for medical use and are marketed to treat patients suffering from a specific pathology. Further work may suggest that they could be used to treat another disease.

For example, this was the case with perindopril, an angiotensin converting enzyme inhibitor (ACE inhibitor) used for a long time against high blood pressure and now used for prevention of cardiac problems in children suffering from Duchenne muscular dystrophy