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Illustration for article: Telethon 2020: 58 290 120 euros!

Telethon 2020: 58 290 120 euros!

At the end of the television broadcast, the counter of the 2020 Telethon shows 58 290 120 euros. Despite the health crisis, which led to the cancellation of a very large number of events in towns and villages, the French people responded positively to this extraordinary Telethon: the one presenting the greatest victories of its history. Behind these victories, there are faces, first names, children, parents, changed lives, regained motions, smiles and laughter, and life who wins.
Illustration for article: The Généthon laboratory, gene therapy pioneer, is 30 years old!

The Généthon laboratory, gene therapy pioneer, is 30 years old!

Généthon, a unique scientific and human adventure, turns 30 this year. Created by a patient organization and funded by the Téléthon, this laboratory has put France at the forefront of genome exploration and of the gene therapy revolution.
Illustration for article: Cure through Innovation 2020 is available online!

Cure through Innovation 2020 is available online!

What is AFM-Telethon? What are its missions? What were the highlights of 2019? The answer is in the Cure through Innovation booklet.
Illustration for article: A European Alliance for Newborn Screening in Spinal Muscular Atrophy

A European Alliance for Newborn Screening in Spinal Muscular Atrophy

Enabling early detection and diagnosis of the disease is the aim of the new European Alliance for Newborn Screening in Spinal Muscular Atrophy (SMA NBS Alliance), launched on August 31st by SMA Europe, of which AFM-Telethon is a member.
Illustration for article: Myositis: A new classification system based on phenotypic, biological and immunological criteria

Myositis: A new classification system based on phenotypic, biological and immunological criteria

Illustration for article: 77 298 024 € raised for the 2020 Téléthon!

77 298 024 € raised for the 2020 Téléthon!

Last December 4th and 5th, the 2020 Telethon took place in a difficult context due to the COVID19 crisis with donations totalling nearly 58.3 million euros by the end of the TV broadcast. A few months later, we are extremely proud to share the exceptional final result of our 2020 fundraising campaign: 77 298 024 euros. Thank you so much!
Illustration for article: First Patient dosed in Clinical Trial of Investigational Gene therapy for Duchenne Muscular Dystrophy

First Patient dosed in Clinical Trial of Investigational Gene therapy for Duchenne Muscular Dystrophy

A first participant was dosed at I-Motion, the pediatric clinical trial platform for neuromuscular diseases located at Trousseau hospital in Paris, as part of the gene therapy trial in Duchenne muscular dystrophy (DMD) conducted by Genethon.
Illustration for article: Genethon, a unique strike force against rare diseases

Genethon, a unique strike force against rare diseases

On February 28, International Rare Disease Day will put the spotlight on the rare diseases community throughout the world. At this occasion, AFM-Telethon revisits thirty years of pioneering research and innovation carried out by its laboratory, Genethon, which has developed a high-level expertise in researching and developing preclinical and clinical gene therapy treatments for rare diseases.
Illustration for article: Thirty years of Genethon: the saga in videos

Thirty years of Genethon: the saga in videos

The laboratory of AFM-Telethon celebrates its 30th anniversary: watch the video series recounting the saga of this one-of-a-kind laboratory, which put France at the forefront of genome exploration, and has supported gene therapy through thick and thin, bringing it to its first successes today. Let us have a look back at this ongoing medical revolution.
Illustration for article: On december 4 and 5, the force of the Téléthon will be with you

On december 4 and 5, the force of the Téléthon will be with you

They are #SoStrong! Families who fight on a daily basis against the disease, researchers who turn genes into medicine, volunteers, donors and partners who, every year, brave the cold… Thanks to them joining forces for the past 30 years, a medical revolution is underway today! Together, let’s keep on giving children and patients the strength to heal!
Illustration for article: World Duchenne Awareness Day: towards a gene therapy trial in France

World Duchenne Awareness Day: towards a gene therapy trial in France

The World Duchenne Awareness Day takes place on September 7th, 2020! After many years of research, hopes for treatments become reality, specifically for Duchenne Muscular Dystrophy, one of Telethon’s most emblematic diseases, which was at the root of parents’ fight and of the creation of AFM-Telethon by the association’s pioneers. A gene therapy trial, stemming from research conducted in Genethon, a Telethon laboratory, should start in France and more broadly in the United Kingdom, Israel and the United States.
Illustration for article: You are great! 87 026 262 euros were raised for the 2019 Telethon !

You are great! 87 026 262 euros were raised for the 2019 Telethon !

Last December 6th and 7th, people all across France rallied in favour of the 2019 Telethon, with donations totalling 74.5 million euros by the end of the television broadcast. Today, a few months later, we are very proud to announce the final result of our 2019 fundraising campaign: 87 026 262 euros. You are great!
Illustration for article: In memory of Jon A Wolff

In memory of Jon A Wolff

It is with great sorrow that we share the sad news of the death of a great researcher, a pioneer of gene therapy and a fellow traveler of the AFM-Telethon. Jon A Wolff died on April 17, 2020 of esophageal cancer, the first signs of which he had detected during a visit to France 18 months earlier.
Illustration for article: Novartis/Avexis invents gene therapy by drawing lots. AFM-Telethon is outraged!

Novartis/Avexis invents gene therapy by drawing lots. AFM-Telethon is outraged!

Novartis has announced a free access program for Zolgensma, the gene therapy approved in the US for spinal muscular atrophy and currently undergoing approval in Europe and Japan. In very specifics ways...
Illustration for article: Telethon 2019: the final counter reaches 74 569 212 euros

Telethon 2019: the final counter reaches 74 569 212 euros

The counter of the 2019 Telethon, which took place on December 6 and 7, displays 74 569 212 euros. A result that will help multiply victories !
Illustration for article: Telethon 2019: let us multiply victories

Telethon 2019: let us multiply victories

The first drugs capable of repairing DNA are here! Gene therapy is no longer a dream, it has become a reality for patients. In 2019, the Telethon celebrates this medical revolution with a fierce determination to multiply Victories, so that one day each patient has the “chance” to receive treatment.
Illustration for article: Gene therapy success in neuromuscular diseases

Gene therapy success in neuromuscular diseases

The world has changed and the terrible diagnosis of spinal muscular atrophy communicated to parents now comes with a word that is full of hope: treatment.
Illustration for article: The “Cure Through Innovation 2019” booklet: all AFM-Téléthon at a glance

The “Cure Through Innovation 2019” booklet: all AFM-Téléthon at a glance

The Cure Through Innovation 2019 booklet is now on line.
Illustration for article: Overview of Myology 2019

Overview of Myology 2019

Myology2019, the sixth edition of the international congress of myology organized by AFM-Telethon, took place in Bordeaux, France, from March 25 to 28.
Illustration for article: 85 844 117 euros - #Telethon2018 #Thankyou #Amazingdonors

85 844 117 euros - #Telethon2018 #Thankyou #Amazingdonors

The final result of the Telethon 2018 reaches 85 844 117 euros*. This extraordinary result, achieved in particularly difficult circumstances, demonstrates once again the utmost loyalty of the French people towards the struggle of affected families.